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Acadia Pharmaceuticals USD 273.57M 201.79M 2025-12
Agios Pharmaceuticals USD -99.11M 8.93M 2026-03
Alnylam Pharmaceuticals USD 205.99M 19.57M 2026-03
BioCryst Pharmaceuticals USD 245.84M 232.95M 2025-12
BioMarin Pharmaceutical USD 105.53M 152.1M 2026-03
Esperion Therapeutics USD 61.83M 93.16M 2025-12
Immunic USD -19.3M 6.28M 2025-12
Insmed USD -328.48M 41.54M 2025-12
Ionis Pharmaceuticals USD -93M 136M 2026-03
Karyopharm Therapeutics USD -102.2M 71.42M 2025-12
Kyowa Hakko Kirin JPY 34.44B 18.16B 2025-12
MacroGenics USD -14.16M 30.98M 2025-12
Moderna USD -1.34B 517M 2026-03
Neurocrine Biosciences USD 153.7M 55.8M 2025-12
PTC Therapeutics USD -134.96M 150.86M 2025-12
Puma Biotechnology USD 20.32M 24.85M 2024-09
Regeneron Pharmaceuticals USD 727.2M 117.4M 2026-03
Sarepta Therapeutics USD -412.23M 232.28M 2025-12
Ultragenyx Pharmaceutical USD -129M 51.41M 2025-12
Vertex Pharmaceuticals USD 1.03B 159.7M 2026-03
Xoma USD -17.24M 33.23M 2024-09